三九養(yǎng)生堂記者 鄧肯·蓋伊 報道
精彩| 復??(fu)旦?(dan)大??(da)學??(xue)附??(fu)屬??(shu)眼??(yan)耳??(er)鼻??(bi)喉?(hou)科??(ke)醫(yī)??(yi)院??(yuan)耳??(er)聾??(long)基??(ji)因??(yin)治??(zhi)療??(liao)團??(tuan)隊??(dui)采??(cai)用?(yong)基??(ji)因??(yin)補?(bu)償??(chang)的??(de)方??(fang)式??(shi)??,將??(jiang)基??(ji)因??(yin)治??(zhi)療??(liao)藥??(yao)物?(wu)通??(tong)過??(guo)微?(wei)創(chuàng)??(chuang)局??(ju)部??(bu)注??(zhu)射??(she)到??(dao)患?(huan)兒??(er)內??(nei)耳??(er)??,彌??(mi)補??(bu)缺??(que)陷??(xian)的??(de)耳?(er)畸??(ji)蛋??(dan)白??(bai)??,從??(cong)而??(er)恢??(hui)復??(fu)或??(huo)改??(gai)善??(shan)OTOF突??(tu)變??(bian)耳??(er)聾??(long)患??(huan)兒??(er)的??(de)聽?(ting)覺??(jiao)和??(he)言??(yan)語?(yu)功??(gong)能??(neng)??。??目?(mu)前??(qian)??,該??(gai)團??(tuan)隊??(dui)已??(yi)納??(na)入??(ru)多??(duo)例??(li)患??(huan)兒??(er)??,臨??(lin)床??(chuang)試??(shi)驗??(yan)結??(jie)果??(guo)表??(biao)明??(ming)??,內??(nei)耳??(er)基?(ji)因??(yin)治??(zhi)療??(liao)策??(ce)略??(lve)在??(zai)耳??(er)聾??(long)患??(huan)者??(zhe)中??(zhong)是?(shi)安??(an)全??(quan)、有??(you)效??(xiao)的??(de)??。該??(gai)研??(yan)究??(jiu)為??(wei)OTOF基??(ji)因??(yin)突??(tu)變??(bian)致??(zhi)聾??(long)患??(huan)者??(zhe)提??(ti)供??(gong)了??(le)特??(te)異??(yi)性??(xing)的??(de)基??(ji)因??(yin)治??(zhi)療??(liao)候??(hou)選??(xuan)藥?(yao)物??(wu)??,是??(shi)遺祝(yi)傳??(chuan)性??(xing)耳?(er)聾??(long)治??(zhi)療??(liao)領?(ling)域?(yu)的??(de)重祝(zhong)要??(yao)突??(tu)破??(po)??。與??(yu)此??(ci)同??(tong)時??(shi)??,在??(zai)術??(shu)前?(qian)評??(ping)估??(gu)、給??(gei)藥??(yao)方??(fang)式??(shi)、術??(shu)中??(zhong)監(jiān)??(jian)控??(kong)、術??(shu)后??(hou)護??(hu)理??(li)等??(deng)方??(fang)面??(mian)??,該?(gai)團??(tuan)隊??(dui)建??(jian)立??(li)了?(le)成??(cheng)熟?(shu)的??(de)臨?(lin)床??(chuang)治??(zhi)療??(liao)方??(fang)案??(an)??,為??(wei)后??(hou)續(xù)??(xu)研??(yan)究??(jiu)及??(ji)臨??(lin)床??(chuang)應??(ying)用??(yong)提??(ti)供??(gong)有??(you)力??(li)支??(zhi)撐??(cheng)???! ‰S?(sui)著??(zhe)生??(sheng)物??(wu)醫(yī)??(yi)藥?(yao)技??(ji)術??(shu)革??(ge)新??(xin)發(fā)??(fa)展??(zhan)??,基??(ji)因??(yin)治??(zhi)療??(liao)被??(bei)認?(ren)為??(wei)是??(shi)根??(gen)治??(zhi)遺??(yi)傳??(chuan)性??(xing)耳?(er)聾??(long)最??(zui)有??(you)潛??(qian)力??(li)和??(he)最??(zui)理??(li)想??(xiang)的??(de)策??(ce)略??(lve)之?(zhi)一??(yi)??。??該??(gai)方??(fang)法??(fa)通??(tong)過??(guo)將?(jiang)正??(zheng)常??(chang)的?(de)基??(ji)因??(yin)或??(huo)有??(you)治??(zhi)療??(liao)作??(zuo)用??(yong)的??(de)基??(ji)因??(yin)導??(dao)入?(ru)靶??(ba)細??(xi)胞??(bao)內??(nei)??,補??(bu)償??(chang)或??(huo)糾??(jiu)正??(zheng)缺?(que)陷??(xian)基??(ji)因??(yin)??,以??(yi)實??(shi)現(xiàn)?(xian)從??(cong)根??(gen)本??(ben)上??(shang)改??(gai)善??(shan)聽??(ting)力??(li)的??(de)目??(mu)標??(biao)??,其??(qi)恢??(hui)復??(fu)的??(de)聽??(ting)力??(li)更?(geng)接??(jie)近??(jin)自??(zi)然??(ran)聲??(sheng)音??(yin)的??(de)狀??(zhuang)態(tài)??(tai)??。
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